Gene Therapy for APOE4 Homozygote of Alzheimer's Disease
Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis
AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis
Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis (LINCL)
Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis
Genotype - Phenotype Correlations of LINCL
Doxycycline for COPD in HIV-Infected Patients
Safety and Efficacy of a Lysophosphatidic Acid Receptor Antagonist in Idiopathic Pulmonary Fibrosis
Study to Assess the Efficacy and Safety of Simtuzumab (GS-6624) in Adults With Idiopathic Pulmonary Fibrosis (IPF) (RAINIER)
A Study of Lebrikizumab in Participants With Idiopathic Pulmonary Fibrosis (IPF)
Phase 3 Study With Ciprofloxacin Dispersion for Inhalation in Non-CF Bronchiectasis (ORBIT-4)
Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA) (AAVance)
