About Us
The Department of Genetic Medicine at Weill Cornell leads a dynamic and innovative translational research program, advancing diverse fields such as Genetic Therapy and Personalized Medicine.
Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease
| Publication Type | Academic Article |
| Authors | De B, Rosenberg JB, Selvan N, Wilson I, Yusufzai N, Greco A, Kaminsky SM, Heier LA, Ricart Arbona RJ, Miranda IC, Monette S, Nair A, Khanna R, Crystal RG, Sondhi D |
| Journal | Human Gene Therapy |
| Volume | 34 |
| Issue | 17-18 |
| Pagination | 905-916 |
| Date Published | 09/19/2023 |
| DOI | 10.1089/hum.2023.067 |
| PubMed ID | 37624739 |
| PubMed Central ID | PMC10517331 |