Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease
| Publication Type | Academic Article |
| Authors | De B, Rosenberg JB, Selvan N, Wilson I, Yusufzai N, Greco A, Kaminsky SM, Heier LA, Ricart Arbona RJ, Miranda IC, Monette S, Nair A, Khanna R, Crystal RG, Sondhi D |
| Journal | Human Gene Therapy |
| Volume | 34 |
| Issue | 17-18 |
| Pagination | 905-916 |
| Date Published | 09/19/2023 |
| DOI | 10.1089/hum.2023.067 |
| PubMed ID | 37624739 |
| PubMed Central ID | PMC10517331 |